Translating Next-Generation Science Into Transformative Gene Therapies
Pediatric central nervous system disorders, such as Dravet syndrome, contribute both to premature mortality as well as to substantial, lifelong disabilities. Encoded is developing transformative precision gene therapies to provide potentially long-lasting and life-changing benefits for people living with these disorders and their families.
What We Do
Our novel targeting and regulation platform enables us to target any cell type that has a unique genetic profile. Encoded product candidates are designed to overcome first-generation gene therapy challenges by conferring potentially unprecedented gene specificity, cell selectivity and/or increased potency.
News and Events
Join Our Journey
Inspire hope, deliver possibility
Our culture is one of relentless patient focus, creativity and scientific exploration. We achieve our vision by championing bold solutions that solve hard problems.