Current treatment paradigms for individuals with severe genetic disorders are focused on managing symptoms rather than addressing the underlying cause. For many, this means frequent treatment and lifelong management, and for some, the benefit of treatment is minimal. With recent technological advancements, progress in this paradigm is possible.
Viral gene therapy offers the potential to deliver life-changing advances, moving away from disease management towards lasting disease modification. This approach targets the underlying genetic alteration within malfunctioning cells to restore normal gene function.
The potential impact of viral gene therapy is profound. For individuals with genetic disorders who have limited treatment options, it offers the potential of lasting benefit to positively impact their lives. Viral gene therapy has made significant progress, but the limitations of existing technology have prevented it from reaching its full potential.
At Encoded, our mission is to realize the potential of genomics-driven precision medicine by overcoming key limitations of viral gene therapy.